UCLA Center for Duchenne Muscular Dystrophy
Who We Are
Duchenne Muscular Dystrophy is one of the most common and devastating genetic diseases of childhood, affecting approximately 1 in 5000 boys. Progressive muscle degeneration leads to loss of ambulation by age 12, loss of upper arm use in the teen years, and heart and respiratory failure leading to death in the 20s.
The Center for Duchenne Muscular Dystrophy at UCLA leads the nation in translational science focused on Duchenne and is the first comprehensive Duchenne clinic in the western United states. A leading group of UCLA scientists, clinicians and researchers is poised to achieve significant advances in research, clinical care and treatments for Duchenne that are improving, and will potentially extend, the lives of those afflicted.
News
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Identifying rare genetic diseases and helping to reinvent modern medicine
Stanley Nelson, MD, has been named the Dr. Allen and Charlotte Ginsburg Endowed Chair in Translational Genomics.

UCLA plays pivotal role in first gene therapy for Duchenne muscular dystrophy
Scientists at the Center for Duchenne Muscular Dystrophy at UCLA have gotten FDA approval for Sarepta' s gene therapy Elevidys.

Rocker Cooper Jones won't let a genetic disorder stop him from making his music
19-year-old UCLA patient Cooper Jones will give a benefit concert for Center for Duchenne Muscular Dystrophy in summer of 2021.

A Sincere Thank You to Our 2019 Generous Supporters
We present the 2019 CDMD Friends and Family Circle list of generous supporters.