About Us

Mission Statement

Established in 2006, the CDMD at UCLA was built as a result of collaborations among UCLA scientists, clinicians and researchers. Its efforts span from education and outreach to cutting- edge research, drug discovery, clinical trials and care. Funding for the CDMD's remarkable achievements to date has come from a combination of research grants and private philanthropy.

The goals of the CDMD are to:

• Identify additional disease modifying drug targets;
• Perform intelligent drug design;
• Improve access and care in the clinical setting; and
• Increase clinical trial participation

Community

Academic, industry, and patient advocacy groups are working together to fast-track FDA regulations for rare disease settings to permit greater translation of potential DMD treatments to the clinic. The surge of new treatments resulted from excellence in basic science and fruitful partnerships between academia and industry, together with efforts from advocacy groups, including the CDMD.