UCLA Researchers Discover Potential Treatment for Muscular Dystrophy

Skeletal muscles without dystrophin (top row) and after dystrophin has been restored (bottom) using the CRISPR/Cas9 platform developed by UCLA scientists.
By The Center for Duchenne Muscular Dystrophy at UCLA
1 min read

Approach Holds Promise for 60 Percent of Patients with the Deadly Disease

April Pyle, Courtney Young, and Melissa Spencer have discovered a potential treatment for Muscular Dystrophy.

Read the UCLA Newsroom press release "Stem cell gene therapy could be key to treating Duchenne muscular dystrophy."